Hope, CRISPR and the race to save a life
成果类型：
News Item
署名作者：
Ledford, Heidi
刊物名称：
Nature
ISSN/ISSBN：
0028-4277
DOI：
10.1038/d41586-024-01716-y
发表日期：
2024-06-13
页码：
284-288
关键词：
摘要：
Researchers in India fought to develop what could have been the first therapy to use gene-editing to halt a rare neurodegenerative disease. The efforts hold lessons for the messy state of modern drug development.