Cell and gene therapy accessibility
成果类型：
Editorial Material
署名作者：
Rouce, Rayne H.; Porteus, Matthew H.
署名单位：
Baylor College of Medicine; Baylor College Medical Hospital; Stanford University; Stanford University
刊物名称：
SCIENCE
ISSN/ISSBN：
0036-8341
DOI：
10.1126/science.ads0252
发表日期：
2024-08-02
页码：
475-475
关键词：
摘要：
Patients with devastating illnesses demonstrate incredible courage in battling their disease. Innovative cell and gene therapies (CGTs), built on decades of research, are changing the lives of those who suffer from conditions ranging from cancer to sickle cell disease to neurologic diseases. Although hailed for their promise and recognized for benefits that will exceed the costs, the high prices of CGTs ($300 thousand to $4 million per dose) leave these therapies out of reach for many. This accessibility problem will only be solved if academia, industry, investors, funders, regulators, and advocacy groups work together to put CGT breakthroughs in the hands of all who stand to benefit.